8th Gene Therapy Development Summit 2025 The Westin Boston Seaport District, Boston

Welcome to the 8th Gene Therapy Development Summit

Transforming the Future of Gene Therapies for Rare and Common Diseases

With 14 new gene therapy approvals in the last 18 months, billion-dollar collaborations, and the development of treatments for more common conditions, the gene therapy field is rapidly gaining momentum and broadening scope beyond rare diseases. Returning to Boston in March, the 8th Gene Therapy Development Summit, formerly known as the Gene Therapy for Rare Disorders Summit, will unite 200+ gene therapy experts to tackle the field’s biggest challenges of achieving genuine scalability and accessibility to meet growing patient demand.

For the first time, this industry-defining meeting will reflect the field’s growing focus on developing therapies for common diseases, whilst addressing existing hurdles in rare and ultra-rare disorders. This is your unparalleled opportunity to delve into:

– The latest global regulatory requirements
– Optimizing routes for CNS
– Ocular and inner ear disorders
– Innovations in capsid engineering and dosing strategies
– Increasing volumetric productivity to reduce CoGs